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Rare Disease Day 2024: Why Do We Care About Rare?
29 February 2024
…February 23, 2024. https://www.ohe.org/publications/appraising-ultra-orphan-drugs-cost-qaly-appropriate-review-evidence/ Sussex J, Rollet P, Garau M, Schmitt C, Kent A, Hutchings A. Multi-Criteria Decision Analysis to Value Orphan Medicines – OHE. Office of Health Economics. Published…