Rare and Orphan Diseases
Publication
Multi-Criteria Decision Analysis to Value Orphan Medicines
1 May 2013
The purpose of this research is to identify the attributes to include in a value framework for orphan medicinal products (OMPs), determine their relative importance using…
Publication
Assessment of the Impact of Orphan Medicinal Products on the European Economy and Society
1 November 2010
This report examines the effect of the European Union’s 1999 Regulation on Orphan Medicinal Products (OMPs) on the European economy and society. This study collected data…
Publication
Access Mechanisms for Orphan Drugs: A Comparative Study of Selected European Countries
1 November 2009
This study compares pricing and reimbursement (P&R) policy for 43 orphan medicinal products (OMPs) across seven EU Member States: France, Germany, Italy, The Netherlands, Spain, Sweden…
Publication
Huntington’s Chorea
1 March 1980
The purpose of this paper is to describe the nature of Huntington’s chorea and to indicate broadly its costs to both society and affected individuals. The…