Search results for: Gene therapies
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Cost-effectiveness Analysis of Gene Therapies for Inherited Eye Disease: Are Current Discounting Approaches Too Short-sighted?
15 February 2023
…discounting to gene therapies could delay or prevent patients from accessing potentially transformative therapies. The discounting challenge is not unique to gene therapies. Other health technologies like cell therapies, vaccines,…
Exploring the Financial Sustainability of Gene Therapies
5 January 2021
…marketing approval and the size of the eligible patient populations will influence the total spend on gene therapies. As different gene therapies generate different kinds of value for the health…
Challenges and Solutions for Budget Impact Analysis of Gene Therapies
10 March 2025
…therapies. When these models are likely to be employed, they should be factored into BIAs to inform decision making, commercial negotiations, and implementation. Share this: Download publication Gene therapies represent…
Are Recommendations for HTA of Gene Therapies Being Achieved?
11 September 2023
…demonstrating significant potential for improvement in the HTA of gene therapies. Share this: Download publication Several challenges are preventing timely access to gene therapies. Based on a review of the…
ISPOR Issue Panel Roundup: Are Our HTA Methods Fit for Purpose for Gene Therapies?
6 June 2022
…gene therapies have the potential to transform lives and provide further benefits for society and the health system. The development of these therapies presents a new combination of challenges and…
ISPOR Europe Round-up: “Gene Therapies: Where High Promise Meets High Uncertainty, How Should HTA Methodologies Appropriately Value and Enable Access?”
8 December 2022
…and discussed actionable recommendations resulting from an expert roundtable. The report identified four broad categories of challenges faced by gene therapies undergoing health technology assessment (HTA): initial assessment of clinical…
Health Technology Assessment of Gene Therapies: Are Our Methods Fit for Purpose?
1 June 2022
…known monogenic (single gene) cause. In contrast to traditional small molecule medicines, gene therapies have the potential to correct underlying genetic defects, offering the potential for transformational health gains rather…
The Promise of Gene Therapies: Are We Ready?
1 April 2021
…of Gene Therapy: Are We Ready? Click to read Gene therapies debate report OUR 5 KEY TAKEAWAYS FROM THE DEBATE Are we ready for gene therapies? It depends who you…
Cell & Gene Therapies: Can We Find Innovative Ways to Pay?
10 May 2023, 9:00am
The curative nature of cell and gene therapies has the potential to transform our entire approach to healthcare. Approvals have so far been in niche indications but the successful application…