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Exploring the Assessment and Appraisal of Regenerative Medicines and Cell Therapy Products: Is the NICE Approach Fit for Purpose?
1 February 2017
In 2016 the University of York undertook a review exercise to determine whether NICE’s existing methods and processes are appropriate for assessment of regenerative medicines. The purpose of this OHE…
ISPOR Europe Round-up: “Gene Therapies: Where High Promise Meets High Uncertainty, How Should HTA Methodologies Appropriately Value and Enable Access?”
8 December 2022
In November, ISPOR Europe was hosted in person for the first time since 2019 at the Austria Centre, Vienna. In front of a full theatre, OHE’s Professor Adrian Towse introduced…
Gene Therapy: Understanding the Science, Assessing the Evidence, and Paying for Value
1 March 2017
This report presents an analysis of the significant clinical potential of gene therapy and the unique challenges in developing and evaluating evidence on their effectiveness and value. Special attention is…
Exploring the Financial Sustainability of Gene Therapies
5 January 2021
Gene therapies directly address the underlying cause of disease, and many of them offer short-term treatment regimens. As a result, they could bring transformative benefits to patients by halting disease…