World Rare Disease Day aims to raise awareness of rare diseases and the impact they can have on patients. This blog explores OHE’s contributions to research into rare diseases and orphan medicines.

A new publication by Kourouklis and Gandjour (2022) investigates the impact of pharmaceutical spending on domestic early-stage pharmaceutical innovation in Europe. They find that European spending does impact the number of patent applications and that European pharmaceutical spending has an impact on European countries attracting early-stage development.

A paradigm shift is occurring in cancer care with the introduction of tumour-agnostic therapies, for which the indication is defined by the molecular signature of the tumour rather than by its location. While promising for patients, healthcare systems are facing major challenges with the clinical and economic assessment of such therapies and subsequent reimbursement decisions.

As Professor Mike Drummond and Professor Bengt Jonnson step down from the OHE Board of Trustees after more than a decade of service, OHE announces the appointment of Professor Margaret Kyle and Professor Werner Brouwer as replacements with Professor Anita Charlesworth becoming chair